Tag Archives: Cystic

Could synthetic molecules provide a general treatment for Cystic Fibrosis?

A new treatment for lung disease in cystic fibrosis (CF) for which there remains no cure could potentially benefit all patients, according to a University of Bristol study published in Chemical Science. The findings are an important step towards a new therapy addressing the fundamental cause of cystic fibrosis. Cystic Fibrosis is a debilitating disease… Read More: Could synthetic molecules provide a general treatment for Cystic Fibrosis? »

Cystic Fibrosis Lung Function Improved With Triple Therapy

November 09, 2018 Share this content: Chloride sweat concentrations and Cystic Fibrosis Questionnaire-Revised scores improved when VX-659 was added to tezacaftor and ivacaftor. Patients with cystic fibrosis with either 1 or 2 Phe508del alleles who were treated with a drug combination of VX-659, tezacaftor, and ivacaftor showed improved forced expiratory volume in 1 second (FEV1),… Read More: Cystic Fibrosis Lung Function Improved With Triple Therapy »

Cystic fibrosis boy, 8, urges firm to lower Orkambi drug price

Image caption Luis Walker wrote to the Prime Minister asking for her help to make the drug available An eight-year-old boy with cystic fibrosis has urged a pharmaceutical firm to lower the price of a drug so it can be made available on the NHS. Luis Walker, from Horam in East Sussex, told Vertex Pharmaceuticals,… Read More: Cystic fibrosis boy, 8, urges firm to lower Orkambi drug… »