A new treatment for lung disease in cystic fibrosis (CF) for which there remains no cure could potentially benefit all patients, according to a University of Bristol study published in Chemical Science. The findings are an important step towards a new therapy addressing the fundamental cause of cystic fibrosis. Cystic Fibrosis is a debilitating disease… Read More »
November 09, 2018 Share this content: Chloride sweat concentrations and Cystic Fibrosis Questionnaire-Revised scores improved when VX-659 was added to tezacaftor and ivacaftor. Patients with cystic fibrosis with either 1 or 2 Phe508del alleles who were treated with a drug combination of VX-659, tezacaftor, and ivacaftor showed improved forced expiratory volume in 1 second (FEV1),… Read More »
Image caption Luis Walker wrote to the Prime Minister asking for her help to make the drug available An eight-year-old boy with cystic fibrosis has urged a pharmaceutical firm to lower the price of a drug so it can be made available on the NHS. Luis Walker, from Horam in East Sussex, told Vertex Pharmaceuticals,… Read More »