Tag Archives: rare

Rituxan Approved for Pediatric Patients With Rare Vasculitis Diseases

TUESDAY, Oct. 1, 2019 — Rituxan (rituximab) injection was granted the first approval for a drug to treat granulomatosis with polyangiitis (GPA) and microscopic polyangiitis (MPA) in combination with glucocorticoids in children 2 years and older, the U.S. Food and Drug Administration announced Friday. The agency noted that pediatric patients with GPA, previously known as… Read More »

The most expensive medicine ever treats a rare condition. The price: $2.13 million – Los Angeles Times

Evelyn Villarreal was one of the first children treated, at 8 weeks. Her family, from Centreville, Va., had lost their first child to spinal muscular atrophy at 15 months. Two years later when Evelyn was born a test showed she also had the disease, so the family enrolled her in the gene therapy study at… Read More »

A Man Contracted a Rare, Fatal Disease From Eating Squirrel Brains

According to a recently-uncovered medical case from 2015, one man may have died after eating one too many squirrels. His penchant for squirrel meat seems to have inadvertently exposed him to an incredibly rare fatal brain disorder, the first time this disorder was ever contracted in the United States. Advertisement – Continue Reading Below Creutzfeldt–Jakob… Read More »